Gene Therapy:
USA / Poland
Target Area Substantia Nigra Pars Compacta & Ventral Tegmental
Here is a collection of video's and articles relevant to the Gene Therapy from USA / Poland which targets the Substantia Nigra Pars Compacta & Ventral Tegmental area of the brain.
They also document the progress made by some of the AADCd children that have received this form of Gene Therapy.
Title: "Experimental Therapy Gives Children With Genetic Disorders A New Chance At Life"
Published: 19/03/2019 KPIX5 News
Country: USA
AADC World Conference 2018
Professor Krystof Bankiewicz & Dr Toni Pearson presentation:
Title: “AADC Krystof Bankiewicz & Toni Pearson - Phase 1 AAV2-hAADC Clinical Trial”
Published 13/12/2018
Country: USA / Poland
AADC World Conference 2014
Dr Toni Pearson presentation
Title: “AADC Gene Therapy Trial & Natural History Study”
Published 23/12/2014
Country: USA / Poland
Title: "Amazing advances in the treatment of childhood Parkinson's"
Published: 17/02/2019
Country: USA / Poland
AADC World Conference 2014
Professor Krystof Bankiewicz presentation
Title: “Overview of AADC Deficiency - AAV2-hAADC Gene Therapy Trials”
Published 23/12/2014
Country: USA / Poland
Title: “Neuroterapi Center - a new gene therapy for the treatment of brain diseases” (Bankiewicz introduction to his polish clinic/lab)
Published: 4/3/2016
Country: Poland
Active Gene Therapy Trial Information:
A Single-Stage, Adaptive, Open-label Dose Escalation Safety and Efficacy Study of AADC deficiency in Paediatric Patients(AADC)
Sponsor : Krystof Bankiewicz
Collaborator: National Institutes of Health (NIH)
Information provided by (Responsible Party):
Professor Krystof Bankiewicz, University of California, San Francisco
This trial is ACTIVE and RECRUITING.
If you are interested in registering for this trial please click on the image to find out more information. The contact email addresses are at the bottom of the link page.