1 Million steps to £1,000,000.00
There are
7000
rare diseases
1 out 2
patients diagnosed with a rare disease is a child
350million
people suffer from a rare disease worldwide
8 out of 10
rare disease are caused by a faulty gene
1 out 2
rare disease do not have a support group
3 out 10
children with a rare disease will not make it to their 5th birthday
95%
of rare disease have no approved treatment
1 out of 10
are affected by
rare disease
8years
is the average wait time for an accurate diagnosis
Rare disease effects more
than
Cancer & AIDS
combined
The campaign...
The AADC Trust is running the '1 Million steps to £1,000,000.00' as part of our #oneRAREstep Campaign to raise money for children suffering from Aromatic Amino Acid Decarboxylase deficiency (AADCd) to access treatment that will significantly alter symptoms and save lives. The pioneering Gene Therapy treatment AAV2-hAADC is performed by Professor Krystof Bankiewicz and Professor Miroslaw Zabek at the Interventional Neurotherapy Center, Brodno Hospital, Poland. This treatment is setting the benchmark for potential future treatments of diseases with single gene defects.
The aim...
We aim to raise £1 million to fund Gene Therapy treatment for our AADCd children. Look how easily this could be obtained...
Just 0.1% of the WORLD population would need to donate only £1
We need to raise
£1 million
The current WORLD population is
7.7 billion
To reach our target just
0.01% of the WORLD
population would
need donate only £1
Just 1.5% of the UK population would need to donate only £1
We need to raise
£1 million
The current UK
population is
66.04 million
To reach our target just
1.5% of the UK
population would
need donate only £1
EVERY £1 has value...
How to get involved...
JustGiving...
You can donate via our #oneRAREstep JustGiving main campaign page or, if there is a particular AADCd effected child that you would like to support, please select their individual personal appeals.
Social Media...
For more information and updates on the Campaign please follow us on our Social Media platforms...
Disclaimer: The AADC Trust reserves the right that in the event it successfully raises the required funds or acquires government funds from the country where a child resides, to cover the treatment we will use any surplus funds raised from their personal page to assist with their off treatment costs such as travel and accommodation. Any remaining funds will be used by the Trust for the purpose of this Campaign, including distributing them to other children registered for the treatment.