Gene Therapy; A Child's Journey

Ted_18
Romain colour

Over fifty AADCd children and young adults from all around the world have now received gene therapy replacement treatment. Many more are likely to follow in their steps as it becomes more accessible.

 

Here we share some of their truly inspirational journeys on the road to this pioneering treatment, pre and post-surgery.  

Hallie on beach.jpg

Meet Hallie ...

Marcus sitting.jpg

Meet Marcus ...

Huzaifah in garden.jpg

Meet Huzaifah ...

Rian.jpg

Meet Rian ...

Ted in highchair.jpg

Meet Ted ...

Paul on slide.JPG

Meet Paul ...

Audrey Home Page_edited.jpg

Meet Audrey ...

Daria image_edited_edited.jpg

Meet Daria ...